Cerebrospinal Fluid and Clinical Profiles in Adult Type 2–3 Spinal Muscular Atrophy Patients Treated with Nusinersen: An 18-Month Single-Centre Experience Article Swipe

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Giammarco Milella , Alessandro Introna , Eustachio D’Errico , Angela Fraddosio , Gaspare Scaglione , Antonella Morea , Maria Ucci , Maddalena Ruggieri , Mariangela Mastrapasqua , Marisa Megna , Filomena Puntillo , Isabella Laura Simone ·

YOU? · · 2021 · Open Access · · DOI: https://doi.org/10.1007/s40261-021-01071-0

Related Topics

Medicine

Neuromuscular Disease

Concepts

SMA* Medicine Spinal muscular atrophy Cerebrospinal fluid Neuromuscular disease Neurodegeneration Internal medicine Creatinine Atrophy Gastroenterology Disease Combinatorics Mathematics

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Type: article
Language: en
Landing Page: https://doi.org/10.1007/s40261-021-01071-0
PDF: https://link.springer.com/content/pdf/10.1007/s40261-021-01071-0.pdf
OA Status: hybrid
Cited By: 20
References: 49
Related Works: 10
OpenAlex ID: https://openalex.org/W3188912134

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OpenAlex ID: https://openalex.org/W3188912134

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DOI: https://doi.org/10.1007/s40261-021-01071-0

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Title: Cerebrospinal Fluid and Clinical Profiles in Adult Type 2–3 Spinal Muscular Atrophy Patients Treated with Nusinersen: An 18-Month Single-Centre Experience

Work title
Type: article

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Language: en

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Publication year: 2021

Year of publication
Publication date: 2021-08-13

Full publication date if available
Authors: Giammarco Milella, Alessandro Introna, Eustachio D’Errico, Angela Fraddosio, Gaspare Scaglione, Antonella Morea, Maria Ucci, Maddalena Ruggieri, Mariangela Mastrapasqua, Marisa Megna, Filomena Puntillo, Isabella Laura Simone

List of authors in order
Landing page: https://doi.org/10.1007/s40261-021-01071-0

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PDF URL: https://link.springer.com/content/pdf/10.1007/s40261-021-01071-0.pdf

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Open access: Yes

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OA status: hybrid

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OA URL: https://link.springer.com/content/pdf/10.1007/s40261-021-01071-0.pdf

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Concepts: SMA*, Medicine, Spinal muscular atrophy, Cerebrospinal fluid, Neuromuscular disease, Neurodegeneration, Internal medicine, Creatinine, Atrophy, Gastroenterology, Disease, Combinatorics, Mathematics

Top concepts (fields/topics) attached by OpenAlex
Cited by: 20

Total citation count in OpenAlex
Citations by year (recent): 2025: 4, 2024: 5, 2023: 7, 2022: 4

Per-year citation counts (last 5 years)
References (count): 49

Number of works referenced by this work
Related works (count): 10

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