Effect of Oral Eliglustat on Splenomegaly in Patients With Gaucher Disease Type 1 Article Swipe
Pramod K. Mistry
,
Elena Lukina
,
Hadhami Ben Turkia
,
Dominick Amato
,
Hagit Baris
,
Majed Dasouki
,
Marwan Ghosn
,
Atul Mehta
,
Seymour Packman
,
Gregory M. Pastores
,
Мilan Petakov
,
Sarit Assouline
,
Manisha Balwani
,
Sumita Danda
,
Evgueniy Hadjiev
,
Andres Ortega
,
Suma P. Shankar
,
María Helena Solano
,
Leorah Ross
,
Jennifer Angell
,
Michel Peterschmitt
·
YOU?
·
· 2015
· Open Access
·
· DOI: https://doi.org/10.1001/jama.2015.459
YOU?
·
· 2015
· Open Access
·
· DOI: https://doi.org/10.1001/jama.2015.459
clinicaltrials.gov Identifier: NCT00891202.
Related Topics
Concepts
Metadata
- Type
- article
- Language
- en
- Landing Page
- https://doi.org/10.1001/jama.2015.459
- OA Status
- green
- Cited By
- 148
- References
- 33
- Related Works
- 10
- OpenAlex ID
- https://openalex.org/W2094632651
All OpenAlex metadata
Raw OpenAlex JSON
- OpenAlex ID
-
https://openalex.org/W2094632651Canonical identifier for this work in OpenAlex
- DOI
-
https://doi.org/10.1001/jama.2015.459Digital Object Identifier
- Title
-
Effect of Oral Eliglustat on Splenomegaly in Patients With Gaucher Disease Type 1Work title
- Type
-
articleOpenAlex work type
- Language
-
enPrimary language
- Publication year
-
2015Year of publication
- Publication date
-
2015-02-17Full publication date if available
- Authors
-
Pramod K. Mistry, Elena Lukina, Hadhami Ben Turkia, Dominick Amato, Hagit Baris, Majed Dasouki, Marwan Ghosn, Atul Mehta, Seymour Packman, Gregory M. Pastores, Мilan Petakov, Sarit Assouline, Manisha Balwani, Sumita Danda, Evgueniy Hadjiev, Andres Ortega, Suma P. Shankar, María Helena Solano, Leorah Ross, Jennifer Angell, Michel PeterschmittList of authors in order
- Landing page
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https://doi.org/10.1001/jama.2015.459Publisher landing page
- Open access
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YesWhether a free full text is available
- OA status
-
greenOpen access status per OpenAlex
- OA URL
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https://doi.org/10.1001/jama.2015.459Direct OA link when available
- Concepts
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Medicine, Placebo, Enzyme replacement therapy, Anemia, Hepatosplenomegaly, Clinical endpoint, Internal medicine, Gastroenterology, Randomized controlled trial, Surgery, Disease, Pathology, Alternative medicineTop concepts (fields/topics) attached by OpenAlex
- Cited by
-
148Total citation count in OpenAlex
- Citations by year (recent)
-
2025: 12, 2024: 10, 2023: 7, 2022: 9, 2021: 12Per-year citation counts (last 5 years)
- References (count)
-
33Number of works referenced by this work
- Related works (count)
-
10Other works algorithmically related by OpenAlex
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| counts_by_year[5].cited_by_count | 18 |
| counts_by_year[6].year | 2019 |
| counts_by_year[6].cited_by_count | 12 |
| counts_by_year[7].year | 2018 |
| counts_by_year[7].cited_by_count | 17 |
| counts_by_year[8].year | 2017 |
| counts_by_year[8].cited_by_count | 21 |
| counts_by_year[9].year | 2016 |
| counts_by_year[9].cited_by_count | 18 |
| counts_by_year[10].year | 2015 |
| counts_by_year[10].cited_by_count | 12 |
| locations_count | 4 |
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| best_oa_location.source.is_in_doaj | False |
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| best_oa_location.source.host_organization_lineage | https://openalex.org/I1299303238 |
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| best_oa_location.pdf_url | |
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| best_oa_location.license_id | |
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| best_oa_location.is_published | False |
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| primary_location.is_oa | False |
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| primary_location.source.type | journal |
| primary_location.source.is_oa | False |
| primary_location.source.issn_l | 0098-7484 |
| primary_location.source.is_core | True |
| primary_location.source.is_in_doaj | False |
| primary_location.source.display_name | JAMA |
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| primary_location.source.host_organization_name | American Medical Association |
| primary_location.source.host_organization_lineage | https://openalex.org/P4310320259 |
| primary_location.license | |
| primary_location.pdf_url | |
| primary_location.version | publishedVersion |
| primary_location.raw_type | journal-article |
| primary_location.license_id | |
| primary_location.is_accepted | True |
| primary_location.is_published | True |
| primary_location.raw_source_name | JAMA |
| primary_location.landing_page_url | https://doi.org/10.1001/jama.2015.459 |
| publication_date | 2015-02-17 |
| publication_year | 2015 |
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| cited_by_percentile_year.max | 100 |
| cited_by_percentile_year.min | 98 |
| countries_distinct_count | 11 |
| institutions_distinct_count | 21 |
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