Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device Article Swipe

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Cristina Olgasi , Chiara Borsotti , Simone Merlin , Thorsten Bergmann , Patrick Bittorf , Adeolu B. Adewoye , Nicholas M. Wragg , Kelcey Patterson , Andrea Calabria , Fabrizio Benedicenti , Alessia Cucci , Alessandra Borchiellini , Berardino Pollio , Eugenio Montini , Delfina M. Mazzuca , Martin Zierau , Alexandra Stolzing , Philip M. Toleikis , Joris Braspenning , Antonia Follenzi ·

YOU? · · 2021 · Open Access · · DOI: https://doi.org/10.1016/j.omtm.2021.10.015

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Viral vector Vector (molecular biology) Virology Medicine Computer science Biology Genetics Recombinant DNA Gene

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Type: article
Language: en
Landing Page: https://doi.org/10.1016/j.omtm.2021.10.015
PDF: http://www.cell.com/article/S2329050121001728/pdf
OA Status: gold
Cited By: 18
References: 85
Related Works: 10
OpenAlex ID: https://openalex.org/W3209882566

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DOI: https://doi.org/10.1016/j.omtm.2021.10.015

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Title: Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device

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Type: article

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Language: en

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Publication year: 2021

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Publication date: 2021-11-03

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Authors: Cristina Olgasi, Chiara Borsotti, Simone Merlin, Thorsten Bergmann, Patrick Bittorf, Adeolu B. Adewoye, Nicholas M. Wragg, Kelcey Patterson, Andrea Calabria, Fabrizio Benedicenti, Alessia Cucci, Alessandra Borchiellini, Berardino Pollio, Eugenio Montini, Delfina M. Mazzuca, Martin Zierau, Alexandra Stolzing, Philip M. Toleikis, Joris Braspenning, Antonia Follenzi

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Landing page: https://doi.org/10.1016/j.omtm.2021.10.015

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PDF URL: https://www.cell.com/article/S2329050121001728/pdf

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Concepts: Viral vector, Vector (molecular biology), Virology, Medicine, Computer science, Biology, Genetics, Recombinant DNA, Gene

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Cited by: 18

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Citations by year (recent): 2025: 3, 2024: 4, 2023: 7, 2022: 4

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References (count): 85

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Related works (count): 10

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