Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping Article Swipe

Paula R. Clemens , Vamshi K. Rao , Anne M. Connolly , Amy D. Harper , Jean K. Mah , Edward C. Smith , Craig M. McDonald , Craig M. Zaidman , Lauren P. Morgenroth , Hironori Osaki , Youhei Satou , Taishi Yamashita , Eric P. Hoffman , for the CINRG DNHS Investigators · YOU? · · 2020 · Open Access · · DOI: https://doi.org/10.1001/jamaneurol.2020.1264 · OA: W3030480398