Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia Article Swipe
Maria Rosa Lidonnici
,
Ylenia Paleari
,
Francesca Tiboni
,
Giacomo Mandelli
,
Claudia Rossi
,
Michela Vezzoli
,
Annamaria Aprile
,
Carsten W. Lederer
,
Alessandro Ambrosi
,
Franck Chanut
,
Francesca Sanvito
,
Andrea Calabria
,
Valentina Poletti
,
Fulvio Mavilio
,
Eugenio Montini
,
Luigi Naldini
,
Patrizia Cristofori
,
Giuliana Ferrari
·
YOU?
·
· 2018
· Open Access
·
· DOI: https://doi.org/10.1016/j.omtm.2018.09.001
YOU?
·
· 2018
· Open Access
·
· DOI: https://doi.org/10.1016/j.omtm.2018.09.001
Related Topics
Concepts
Genetic enhancement
Biology
Vector (molecular biology)
Thalassemia
Viral vector
Clinical trial
Cancer research
Stem cell
Gene
Vectors in gene therapy
Medicine
Oncology
Bioinformatics
Computational biology
Immunology
Genetics
Recombinant DNA
Metadata
- Type
- article
- Language
- en
- Landing Page
- https://doi.org/10.1016/j.omtm.2018.09.001
- http://www.cell.com/article/S2329050118300901/pdf
- OA Status
- gold
- Cited By
- 23
- References
- 76
- Related Works
- 10
- OpenAlex ID
- https://openalex.org/W2889821345
All OpenAlex metadata
Raw OpenAlex JSON
- OpenAlex ID
-
https://openalex.org/W2889821345Canonical identifier for this work in OpenAlex
- DOI
-
https://doi.org/10.1016/j.omtm.2018.09.001Digital Object Identifier
- Title
-
Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-ThalassemiaWork title
- Type
-
articleOpenAlex work type
- Language
-
enPrimary language
- Publication year
-
2018Year of publication
- Publication date
-
2018-09-13Full publication date if available
- Authors
-
Maria Rosa Lidonnici, Ylenia Paleari, Francesca Tiboni, Giacomo Mandelli, Claudia Rossi, Michela Vezzoli, Annamaria Aprile, Carsten W. Lederer, Alessandro Ambrosi, Franck Chanut, Francesca Sanvito, Andrea Calabria, Valentina Poletti, Fulvio Mavilio, Eugenio Montini, Luigi Naldini, Patrizia Cristofori, Giuliana FerrariList of authors in order
- Landing page
-
https://doi.org/10.1016/j.omtm.2018.09.001Publisher landing page
- PDF URL
-
https://www.cell.com/article/S2329050118300901/pdfDirect link to full text PDF
- Open access
-
YesWhether a free full text is available
- OA status
-
goldOpen access status per OpenAlex
- OA URL
-
https://www.cell.com/article/S2329050118300901/pdfDirect OA link when available
- Concepts
-
Genetic enhancement, Biology, Vector (molecular biology), Thalassemia, Viral vector, Clinical trial, Cancer research, Stem cell, Gene, Vectors in gene therapy, Medicine, Oncology, Bioinformatics, Computational biology, Immunology, Genetics, Recombinant DNATop concepts (fields/topics) attached by OpenAlex
- Cited by
-
23Total citation count in OpenAlex
- Citations by year (recent)
-
2025: 2, 2024: 1, 2023: 4, 2022: 2, 2020: 5Per-year citation counts (last 5 years)
- References (count)
-
76Number of works referenced by this work
- Related works (count)
-
10Other works algorithmically related by OpenAlex
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| referenced_works | https://openalex.org/W2782917400, https://openalex.org/W2764213443, https://openalex.org/W2142159826, https://openalex.org/W2089319449, https://openalex.org/W2593923181, https://openalex.org/W2030600603, https://openalex.org/W1986677646, https://openalex.org/W2789811792, https://openalex.org/W1873308820, https://openalex.org/W4235834002, https://openalex.org/W2136274459, https://openalex.org/W2802087233, https://openalex.org/W2107046588, https://openalex.org/W1966530560, https://openalex.org/W2130174662, https://openalex.org/W2092633851, https://openalex.org/W2061645642, https://openalex.org/W2160374077, https://openalex.org/W2031176947, https://openalex.org/W2093537780, https://openalex.org/W2114634050, https://openalex.org/W2416289241, https://openalex.org/W2111586718, https://openalex.org/W1986316662, https://openalex.org/W2093750771, https://openalex.org/W2073371053, https://openalex.org/W2015378087, https://openalex.org/W2111444354, https://openalex.org/W1997170085, https://openalex.org/W2116613468, https://openalex.org/W2020819071, https://openalex.org/W1499270334, https://openalex.org/W2029161351, https://openalex.org/W1984320737, https://openalex.org/W2045995615, https://openalex.org/W2037797928, https://openalex.org/W2133305859, https://openalex.org/W2011686157, https://openalex.org/W1980878206, https://openalex.org/W1973534046, https://openalex.org/W1938966535, https://openalex.org/W2770876878, https://openalex.org/W2053524220, https://openalex.org/W2168164014, https://openalex.org/W2140777578, https://openalex.org/W2527156470, https://openalex.org/W2141570423, https://openalex.org/W2152094817, https://openalex.org/W2070876549, https://openalex.org/W6716489641, https://openalex.org/W2129406289, https://openalex.org/W1972420656, https://openalex.org/W6630991827, https://openalex.org/W4242914083, https://openalex.org/W1975590431, https://openalex.org/W2119324304, https://openalex.org/W1982786506, https://openalex.org/W2137440275, https://openalex.org/W2323613689, https://openalex.org/W2085823224, https://openalex.org/W1985832579, https://openalex.org/W2028478786, https://openalex.org/W2137495771, https://openalex.org/W2033844621, https://openalex.org/W2084782325, https://openalex.org/W2009078306, https://openalex.org/W2110794606, https://openalex.org/W2107277218, https://openalex.org/W2151782036, https://openalex.org/W2170551349, https://openalex.org/W2097795961, https://openalex.org/W1521286240, https://openalex.org/W2029255163, https://openalex.org/W2080939506, https://openalex.org/W1529296939, https://openalex.org/W1964184380 |
| referenced_works_count | 76 |
| abstract_inverted_index | |
| cited_by_percentile_year.max | 99 |
| cited_by_percentile_year.min | 90 |
| countries_distinct_count | 4 |
| institutions_distinct_count | 18 |
| citation_normalized_percentile.value | 0.90094074 |
| citation_normalized_percentile.is_in_top_1_percent | False |
| citation_normalized_percentile.is_in_top_10_percent | True |