Towards a one‐time cure for Fabry disease: Lentivirus‐mediated haematopoietic stem and progenitor cell gene therapy Article Swipe

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Rina Kansal ·

YOU? · · 2025 · Open Access · · DOI: https://doi.org/10.1002/ctd2.70042

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Haematopoiesis Genetic enhancement Progenitor cell Lentivirus Stem cell Disease Biology Gene Virology Medicine Immunology Cancer research Genetics Internal medicine Human immunodeficiency virus (HIV) Viral disease

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Type: article
Language: en
Landing Page: https://doi.org/10.1002/ctd2.70042
PDF: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/ctd2.70042
OA Status: gold
References: 10
Related Works: 10
OpenAlex ID: https://openalex.org/W4408377438

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OpenAlex ID: https://openalex.org/W4408377438

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DOI: https://doi.org/10.1002/ctd2.70042

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Title: Towards a one‐time cure for Fabry disease: Lentivirus‐mediated haematopoietic stem and progenitor cell gene therapy

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Type: article

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Language: en

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Publication year: 2025

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Publication date: 2025-03-11

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Authors: Rina Kansal

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Landing page: https://doi.org/10.1002/ctd2.70042

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OA URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/ctd2.70042

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Concepts: Haematopoiesis, Genetic enhancement, Progenitor cell, Lentivirus, Stem cell, Disease, Biology, Gene, Virology, Medicine, Immunology, Cancer research, Genetics, Internal medicine, Human immunodeficiency virus (HIV), Viral disease

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