PharmacoEconomics • Vol 42 • No 3
Using Real-World Data to Inform Value-Based Contracts for Cell and Gene Therapies in Medicaid
November 2023 • Antal Zemplényi, Jim Leonard, Michael J. DiStefano, Kelly E. Anderson, Garth Wright, Nicholas D. Mendola, Kavita V. Nair, R. Brett McQueen
Real-world data indicates substantial uncertainty and extended payback periods for gene therapy costs. Utilizing real-world data, Medicaid can negotiate value-based contracts to manage budget fluctuations, share risk with manufacturers, and enhance patient access to innovative treatments.