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View article: Validation of a quantitative cell-based relative potency assay for LUXTURNA
Validation of a quantitative cell-based relative potency assay for LUXTURNA Open
Voretigene neparvovec-rzyl (Luxturna) is an AAV2 vector (AAV2-hRPE65v2) that expresses a cDNA encoding the human retinal pigment epithelium-specific 65 kDa protein (RPE65). It has been approved for the treatment of visual deficits associat…