Niusha Shafaei
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View article: SAT-213 Trial of Vosoritide for Treatment of Short Stature in Turner syndrome: Preliminary Data
SAT-213 Trial of Vosoritide for Treatment of Short Stature in Turner syndrome: Preliminary Data Open
Disclosure: R. Kanakatti Shankar: RKS has received research funding from BioMarin Pharmaceutical Inc., is a consultant for BioMarin, with fees paid to her institution.. N. Shafaei: None. A. Zhang: None. K. Pitner: None. N. Dham: None. A.N.…
View article: Vosoritide treatment for children with hypochondroplasia: a phase 2 trial
Vosoritide treatment for children with hypochondroplasia: a phase 2 trial Open
This study was supported by an investigator-initiated grant from BioMarin Pharmaceutical.
View article: O03: Vosoritide increases growth velocity in hypochondroplasia: Phase 2 trial results
O03: Vosoritide increases growth velocity in hypochondroplasia: Phase 2 trial results Open
Hypochondroplasia is a rare skeletal dysplasia resulting in disproportionate short stature and is due to activating variants in FGFR3. It has an estimated prevalence of between 1 to 9 per 100,000 people. Vosoritide is a C-type natriuretic …